Genome.gov: Genetics Glossary – Gene Therapy
FDA: How Gene Therapy Can Cure or Treat Diseases
National Hemophilia Foundation: Future Therapies – Frequently Asked Questions
National Hemophilia Foundation: Future Therapies
Dovepress: The Patient Experience of Gene Therapy for Hemophilia: Qualitative Interviews with Trial Patients
Orphanet Journal of Rare Diseases: The experiences of people with haemophilia and their families of gene therapy in a clinical trial setting: regaining control, the Exigency study
